Rare Diseases
News
Unexplained collapse unveils rare blood disorder
Acquired TTP often appears to arise in connection with either an immune trigger, such as a viral infection, or immune dysregulation associated...
News
FDA approves first tx for rare, deadly clotting disorder
First drug to treat TTP. a rare, lethal blood clotting disorder, has been greenlighted by the FDA.
News
Short steroid taper tested with tocilizumab for giant cell arteritis
Results from a pilot study examining a shortened prednisone taper of 8 weeks’ length rather than 26 weeks suggest it may be possible to reduce...
News
RNA therapeutics will ‘change everything’ in epilepsy
“We now have the potential to change the way genetic epilepsies are treated by addressing the underlying genetic cause of the disease instead of...
Commentary
Male patients with breast cancer: Special considerations and gender-specific concerns
Even the materials that we have are gender specific. I think those things all together can certainly contribute to a man feeling like a fish out...
News
FDA approves first tocilizumab biosimilar
Tocilizumab-bavi (Tofidence) will offer a lower-cost option for patients with autoimmune conditions, the drug manufacturer, Biogen, stated.
Conference Coverage
Triple therapy boosts anaplastic thyroid cancer survival
"The very long median overall survival in the study's neoadjuvant group is quite remarkable for a group of patients who used to have a very poor...
Case Reports
Idiopathic Granulomatous Lobular Mastitis: A Mimicker of Inflammatory Breast Cancer
Idiopathic granulomatous lobular mastitis (IGLM) is a rare, chronic inflammatory breast disease first described in 1972...
News
FDA okays first-ever new drug for rare bone disorder
The drug reduced annualized heterotopic ossification volume by 54%.
News
Myasthenia gravis drug gets FDA nod
Rozanolixizumab is the first FDA-approved treatment for adults with both subtypes.