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Gene therapy is a contemporary therapeutic intervention with recent positive results and regulatory approvals either completed or expected in the next several years for various conditions. In this supplement, learn more about:
- Basic principles of gene therapy
- In vivo vs ex vivo methods of gene transfer
- Vector types
- Clinical Considerations
About the Author
John Pasi, MB, ChB, PhD
Professor of Haemostasis and Thrombosis
Barts and The London School of Medicine and Dentistry
Haemophilia Centre
London, UK